Conditions / Genetic

mucopolysaccharidosis I

info · Genetic · ICD-10: E76.0

A mucopolysaccharidosis characterized by a deficiency of the lysosomal enzyme alpha-L-iduronidase.

Medications that may treat it

laronidase

Also known as: Hurler syndrome; Hurler-Scheie syndrome; Lipochondrodystrophy; MPS I - Hurler syndrome; Mucopolysaccharidosis, MPS-I