Conditions / Genetic

mucopolysaccharidosis Ih/s

info · Genetic · ICD-10: E76.02

A mucopolysaccharidosis I characterized by an intermediate severity of symptoms including short stature, corneal clouding, joint stiffening, umbilical hernia, dysostosis multiplex, hepatosplenomegaly, and little to no intellectual dysfunction that has_material

A mucopolysaccharidosis I characterized by an intermediate severity of symptoms including short stature, corneal clouding, joint stiffening, umbilical hernia, dysostosis multiplex, hepatosplenomegaly, and little to no intellectual dysfunction that has_material_basis_in homozygous or compound heterozygous mutation in the IDUA gene on chromosome 4p16.3.

Signs and symptoms

  • Corneal opacity
  • Inguinal hernia
  • Camptodactyly of finger
  • Thenar muscle atrophy
  • Heparan sulfate excretion in urine
  • Joint stiffness
  • Umbilical hernia
  • Dysostosis multiplex
  • Dermatan sulfate excretion in urine
  • Contracture of the distal interphalangeal joint of the fingers

Medications that may treat it

laronidase

Also known as: MPS1H/S; MPSIH/S; Mucopolysaccharidosis type 1H/S